AAV Serotypes available

 

Capsid mutations

Cell tropism

References

AAV1   RPE Burger et al.
AAV2   RPE, RGC Acland et al.; Guy et al.1
AAV2(444) Y444F RPE, RGC Petrs-Silva et al.1
AAV2(double) Y444F+Y730F RPE, RGC Petrs-Silva et al.2
AAV2(triple) Y444F+Y500F+Y730F RGC, PR Petrs-Silva et al.2
AAV2(quad) Y272F+Y444F+Y500F+Y730F RGC, PR, VEC Petrs-Silva et al.2; Cai et al.
AAV2(sext) Y252F+Y272F+Y444F+Y500F+Y704F+Y730F Kidney Petrs-Silva et al.2; Qi, YF et al.
AAV2(sept) Y252F+Y272F+Y444F+Y500F+Y700F+Y704F+Y730F RGC, PR, VEC Petrs-Silva et al.2; Ruan et al.
AAV5   PR, RPE, Cornea, Brain Boye et al.1; Beltran et al.; Mohan et al.; Burger et al.
AAV5(719) Y719F PR, RPE Michalakis et al.
AAV8   PR Allocca et al.
AAV8(447) Y447F PR Petrs-Silva et al.1
AAV8(733) Y733F PR, RPE Petrs-Silva et al.1; Pang et al.; Boye et al.2Deng et al.
AAV9   PR, Liver, Heart Lebherz et al.; Sarkar et al.